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205 clinical-stage companies. Search or filter to narrow the list.

Ticker Company Therapeutic areas Lead stage Programs
FDMT 4D Molecular Therapeutics OphthalmologyRespiratory Rare Phase 3 5
ABSI Absci DermatologyGI/Hepatology+1 Phase 1 6
ACIU AC Immune Neurology Rare Phase 3 10
ACHV Achieve Life Sciences NDA Submitted 2
ACRS Aclaris Therapeutics DermatologyGI/Hepatology+1 Rare Phase 2 8
ACRV Acrivon Therapeutics Oncology Phase 2 6
ACTU Actuate Therapeutics Oncology Phase 2 4
ABOS Acumen Pharmaceuticals Neurology Phase 2 4
ADAG Adagene Oncology Phase 2 10
ADCT ADC Therapeutics Oncology Approved 5
ACET Adicet Bio ImmunologyNeurology+2 Rare Phase 1 8
ADMA Adma Biologics ImmunologyInfectious Disease Rare Approved 4
AGMB Agomab Therapeutics ImmunologyRespiratory Rare Phase 2 4
AKBA Akebia Therapeutics HematologyOphthalmology+2 Rare Approved 10
AKTS Aktis Oncology Oncology Phase 1 10
ALDX Aldeyra Therapeutics DermatologyOncology+1 Rare NDA Submitted 7
ALLO Allogene Therapeutics ImmunologyOncology Rare Phase 2 10
DRTS Alpha Tau Medical Oncology Phase 2 5
ATHE Alterity Therapeutics Neurology Rare Phase 2 2
ALT Altimmune GI/HepatologyMetabolic+1 Phase 3 3
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare Phase 3 5
ANAB AnaptysBio DermatologyGI/Hepatology+2 Rare Approved 6
ANIX Anixa Biosciences Oncology Phase 1 3
ANNX Annexon HematologyNeurology+2 Rare Phase 3 6
APGE Apogee Therapeutics DermatologyGI/Hepatology+1 Rare Phase 2 9
APVO Aptevo Therapeutics Oncology Phase 1 8
RCUS Arcus Biosciences DermatologyImmunology+1 Phase 3 6
ARDX Ardelyx GI/HepatologyRenal Approved 4
ARTV Artiva Biotherapeutics DermatologyImmunology+2 Rare Phase 2 14
ARVN Arvinas NeurologyOncology Rare Approved 12
ATAI Atai Beckley Neurology Phase 2 5
AUTL Autolus Therapeutics HematologyImmunology+3 Rare Approved 12
BEAM Beam Therapeutics HematologyMetabolic+1 Rare Phase 2 6
BLTE Belite Bio MetabolicOphthalmology Rare NDA Submitted 6
BCAX Bicara Therapeutics Oncology Phase 2 4
BIOA BioAge Labs CardiovascularOphthalmology Phase 2 2
BMEA Biomea Fusion MetabolicOncology Phase 2 4
BCTX BriaCell Therapeutics Oncology Phase 3 7
BBOT BridgeBio Oncology Therapeutics Oncology Phase 1 8
CCCC C4 Therapeutics Oncology Phase 2 2
CABA Cabaletta Bio DermatologyImmunology+2 Rare Phase 1 8
CAPR Capricor Therapeutics Infectious DiseaseNeurology Rare NDA Submitted 2
CRDL Cardiol Therapeutics Cardiovascular Rare Phase 3 4
CRBU Caribou Biosciences Oncology Phase 1 4
RNAC Cartesian Therapeutics ImmunologyNeurology+1 Rare Phase 3 4
CLDX Celldex Therapeutics DermatologyImmunology+1 Phase 3 7
CLRB Cellectar Biosciences Oncology Phase 2 6
IPSC Century Therapeutics ImmunologyMetabolic+1 Rare Phase 1 9
CRVO CervoMed Neurology Rare Phase 3 4
CGON CG Oncology Oncology NDA Submitted 1
CING Cingulate Neurology NDA Submitted 1
CLNN Clene Neurology Rare Phase 3 5
CLYM Climb Bio HematologyImmunology+1 Rare Phase 2 7
COGT Cogent Biosciences HematologyOncology Rare NDA Submitted 7
CGTX Cognition Therapeutics Neurology Phase 2 2
CHRS Coherus Oncology Oncology Approved 3
CMPS COMPASS Pathways Neurology NDA Submitted 3
CMPX Compass Therapeutics Oncology Phase 2 9
CGEN Compugen Oncology Phase 3 7
CNTB Connect Biopharma Respiratory Phase 2 4
CRVS Corvus Pharmaceuticals DermatologyOncology Phase 3 4
CBIO Crescent Biopharma Oncology Phase 2 10
CRNX Crinetics Pharmaceuticals MetabolicOncology Rare Approved 6
CUE Cue Biopharma ImmunologyOncology Phase 2 6
CGEM Cullinan Therapeutics HematologyImmunology+2 Rare NDA Submitted 10
HELP Cybin Neurology Phase 3 3
CYDY CytoDyn NeurologyOncology Phase 2 3
CTMX CytomX Therapeutics Oncology Phase 1 6
DBVT DBV Technologies Immunology NDA Submitted 2
DFTX Definium Therapeutics Neurology Phase 3 4
DYN Dyne Therapeutics MetabolicNeurology Rare NDA Submitted 10
EIKN Eikon Therapeutics Oncology Phase 2 13
ELDN Eledon Pharmaceuticals ImmunologyNeurology Rare Phase 2 2
ELTX Elicio Therapeutics Oncology Phase 2 6
ELOX Eloxx Pharmaceuticals DermatologyRenal Rare Phase 2 4
ENTA Enanta Pharmaceuticals DermatologyImmunology+1 Phase 2 6
ENTX Entera Bio GI/HepatologyMetabolic Rare Phase 2 4
ERAS Erasca Oncology Phase 1 3
ETON Eton Pharmaceuticals GI/HepatologyInfectious Disease+2 Rare Approved 14
EVMN Evommune DermatologyImmunology+1 Phase 2 6
EXEL Exelixis CardiovascularOncology Approved 22
EYPT EyePoint Ophthalmology Phase 3 3
FHTX Foghorn Therapeutics Oncology Phase 1 5
FBRX Forte Biosciences DermatologyGI/Hepatology Phase 2 3
FBIO Fortress Biotech DermatologyHematology+2 Rare Approved 12
GUTS Fractyl Health Metabolic Phase 3 3
GANX Gain Therapeutics MetabolicNeurology Rare Phase 1 5
GNLX Genelux Oncology Phase 3 3
GERN Geron Oncology Approved 3
GHRS GH Research NeurologyWomen's Health Phase 2 4
GOSS Gossamer Bio Cardiovascular Rare Phase 3 4
GRCE Grace Therapeutics Neurology NDA Submitted 1
GLSI Greenwich LifeSciences Oncology Phase 3 1
IMTX Immatics Oncology Phase 2 8
IMMX Immix Biopharma Hematology Rare Phase 1 1
IMRX Immuneering Oncology Phase 3 5
IMUX Immunic GI/HepatologyNeurology Phase 3 4
IBRX ImmunityBio Infectious DiseaseOncology Approved 16
IMNM Immunome Oncology Rare NDA Submitted 9
IMVT Immunovant ImmunologyNeurology Rare Phase 3 6
INAB IN8bio ImmunologyOncology Phase 2 6
IXHL Incannex Healthcare ImmunologyNeurology+1 Phase 2 3
INMB Inmune Bio DermatologyOncology Rare Phase 2 2
INSM Insmed CardiovascularDermatology+2 Rare Approved 9
NTLA Intellia Therapeutics CardiovascularImmunology Rare NDA Submitted 3
JBIO Jade Biosciences ImmunologyRenal Rare Phase 2 4
JANX Janux Therapeutics Oncology Phase 1 3
KAPA Kairos Pharma Oncology Phase 2 9
KPRX Kiora Pharmaceuticals Ophthalmology Rare Phase 2 4
KOD Kodiak Sciences Ophthalmology Phase 3 8
KURA Kura Oncology MetabolicOncology Approved 12
KYMR Kymera Therapeutics DermatologyRespiratory Rare Phase 2 4
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare NDA Submitted 7
LRMR Larimar Therapeutics Neurology Rare NDA Submitted 1
LEGN Legend Biotech Oncology Rare Approved 8
LENZ LENZ Therapeutics Ophthalmology Approved 1
LXEO Lexeo Therapeutics CardiovascularNeurology Rare Phase 1 8
LCTX Lineage Cell Therapeutics NeurologyOphthalmology Rare Phase 2 5
LGVN Longeveron CardiovascularMetabolic+1 Rare Phase 2 4
MAIA MAIA Biotechnology Oncology Phase 3 7
MPLT MapLight Therapeutics Neurology Phase 2 6
MRKR Marker Therapeutics Oncology Phase 1 4
MDNAF Medicenna Therapeutics Oncology Phase 2 9
MIST Milestone Pharmaceuticals Cardiovascular Approved 2
INKT MiNK Therapeutics ImmunologyOncology+1 Rare Phase 2 7
GLUE Monte Rosa Therapeutics CardiovascularDermatology+2 Rare Phase 2 6
MLTX MoonLake Immunotherapeutics DermatologyImmunology Rare Phase 3 4
NKTR Nektar Therapeutics DermatologyImmunology+2 Phase 3 11
NGEN NervGen Pharma Neurology Phase 1 3
NGNE Neurogene Neurology Rare Phase 3 1
NRSN NeuroSense Therapeutics Neurology Rare Phase 2 3
NAMS NewAmsterdam Pharma CardiovascularMetabolic+1 NDA Submitted 6
NKTX Nkarta ImmunologyNeurology+1 Rare Phase 1 8
NBP NovaBridge Biosciences OncologyOphthalmology Phase 2 6
NRXP NRX Pharmaceuticals Neurology NDA Submitted 5
NRIX Nurix Therapeutics ImmunologyNeurology+1 Phase 3 16
NVCT Nuvectis Pharma HematologyOncology+1 Rare Phase 3 8
OCGN Ocugen Infectious DiseaseOphthalmology Rare Phase 3 12
OCS Oculis Holding NeurologyOphthalmology Rare Phase 3 4
OMER Omeros HematologyNeurology+2 Rare Approved 6
IRD Opus Genetics Ophthalmology Rare Approved 14
ORKA Oruka Therapeutics DermatologyImmunology Rare Phase 2 7
OTLK Outlook Therapeutics Ophthalmology Approved 3
OVID Ovid Therapeutics Neurology Rare Phase 2 4
PALI Palisade Bio Immunology Phase 1 3
KTTA Pasithea Therapeutics NeurologyOncology Rare Phase 1 4
PEPG PepGen Neurology Rare Phase 2 1
CATX Perspective Therapeutics Oncology Phase 1 4
PHIO Phio Pharmaceuticals Oncology Phase 1 4
PMVP PMV Pharmaceuticals Oncology Phase 2 7
PYPD PolyPid Infectious DiseaseOncology NDA Submitted 2
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare Phase 1 5
PCSA Processa Pharmaceuticals GI/HepatologyImmunology+2 Rare Phase 2 7
PMN ProMIS Neurosciences Neurology Rare Phase 1 6
TARA Protara Therapeutics DermatologyMetabolic+1 Rare Phase 2 3
QNRX Quoin Pharmaceuticals DermatologyImmunology Rare Phase 2 4
RLAY Relay Therapeutics DermatologyOncology Rare NDA Submitted 4
RLMD Relmada Therapeutics MetabolicNeurology+1 Rare Phase 2 4
REPL Replimune Group Oncology Approved 5
RVPH Reviva Pharmaceuticals CardiovascularDermatology+2 Rare Phase 3 10
RYTM Rhythm Pharmaceuticals Metabolic Rare Approved 13
RCKT Rocket Pharmaceuticals CardiovascularImmunology Rare Approved 4
SABS SAB Biotherapeutics Metabolic Phase 2 1
SGMT Sagimet Biosciences DermatologyMetabolic NDA Submitted 3
SANA Sana Biotechnology MetabolicOncology Phase 1 4
SRPT Sarepta Therapeutics NeurologyRespiratory Rare Approved 10
SCYX Scynexis Infectious DiseaseRenal Rare Approved 5
SLS SELLAS Life Sciences Group Oncology Phase 3 9
SION Sionna Therapeutics Respiratory Rare Phase 2 5
SLDB Solid Biosciences CardiovascularNeurology Rare Phase 3 6
SPRB Spruce Biosciences Metabolic Rare Preclinical 2
SYRE Spyre Therapeutics DermatologyImmunology Rare Phase 2 13
GPCR Structure Therapeutics MetabolicRespiratory Rare Phase 3 5
SMMT Summit Therapeutics Oncology NDA Submitted 4
STRO Sutro Biopharma Oncology Phase 1 4
TNGX Tango Therapeutics Oncology Phase 1 4
TSHA Taysha Gene Therapies Neurology Rare Phase 3 4
TECX Tectonic Therapeutic Cardiovascular Rare Phase 2 3
TENX Tenax Therapeutics Cardiovascular Rare Phase 3 2
TGTX Tg Therapeutics Neurology Rare Approved 6
TVTX Travere Therapeutics MetabolicRenal Rare Approved 7
TTRX Turn Therapeutics DermatologyInfectious Disease Rare Phase 2 4
TYRA Tyra Biosciences MetabolicOncology Rare Phase 2 5
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare Approved 12
UNCY Unicycive Therapeutics Renal NDA Submitted 2
QURE uniQure HematologyMetabolic+1 Rare Approved 4
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare Approved 29
PCVX Vaxcyte Infectious Disease Phase 3 6
VERA Vera Therapeutics Infectious DiseaseRenal Rare Approved 6
VSTM Verastem Oncology Approved 5
VRCA Verrica Pharmaceuticals DermatologyOncology Approved 3
VKTX Viking Therapeutics MetabolicNeurology Rare Phase 3 8
VIR Vir Biotechnology Infectious DiseaseOncology Rare Phase 3 10
VRDN Viridian Therapeutics ImmunologyOphthalmology Approved 5
VOR Vor Biopharma ImmunologyNeurology Rare Phase 3 2
VYGR Voyager Therapeutics MetabolicNeurology Rare Phase 1 9
VTVT vTv Therapeutics MetabolicRespiratory Rare Phase 3 8
WVE Wave Life Sciences MetabolicNeurology+1 Rare Phase 2 5
XNCR Xencor HematologyImmunology+4 Rare Approved 36
XENE Xenon Pharmaceuticals Neurology Rare Phase 3 8
XERS Xeris Biopharma MetabolicNeurology Rare Approved 4
ZBIO Zenas BioPharma DermatologyImmunology+2 Rare NDA Submitted 11
ZNTL Zentalis Pharmaceuticals Oncology Phase 3 1
ZURA Zura Bio DermatologyImmunology Rare Phase 2 5
ZYME Zymeworks OncologyRespiratory Approved 11