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174 clinical-stage companies. Search or filter to narrow the list.
| Ticker | Company | Therapeutic areas | Lead stage | Programs |
|---|---|---|---|---|
| FDMT | 4D Molecular Therapeutics | OphthalmologyRespiratory Rare | Phase 3 | 5 |
| ABSI | Absci | DermatologyGI/Hepatology+1 | Phase 1 | 7 |
| ACIU | AC Immune | Neurology Rare | Phase 3 | 11 |
| ACRS | Aclaris Therapeutics | DermatologyRespiratory | Phase 2 | 7 |
| ACRV | Acrivon Therapeutics | Oncology | Phase 2 | 5 |
| ACTU | Actuate Therapeutics | Oncology | Phase 2 | 8 |
| ABOS | Acumen Pharmaceuticals | Neurology | Phase 2 | 4 |
| ADAG | Adagene | Oncology | Phase 2 | 9 |
| ADCT | ADC Therapeutics | Oncology | Approved | 5 |
| ADMA | Adma Biologics | Infectious Disease | Approved | 4 |
| AGMB | Agomab Therapeutics | ImmunologyRespiratory Rare | Phase 2 | 4 |
| AKBA | Akebia Therapeutics | HematologyOphthalmology+2 Rare | Approved | 10 |
| AKTS | Aktis Oncology | Oncology | Phase 1 | 9 |
| ALDX | Aldeyra Therapeutics | DermatologyOncology+1 Rare | NDA Submitted | 8 |
| ALLO | Allogene Therapeutics | ImmunologyOncology Rare | Phase 2 | 12 |
| DRTS | Alpha Tau Medical | Oncology | Phase 2 | 5 |
| ATHE | Alterity Therapeutics | Neurology Rare | Phase 3 | 2 |
| ALT | Altimmune | GI/HepatologyMetabolic+1 | Phase 2 | 3 |
| AMLX | Amylyx Pharmaceuticals | MetabolicNeurology Rare | Phase 3 | 5 |
| ANAB | AnaptysBio | DermatologyGI/Hepatology+2 Rare | Approved | 6 |
| ANNX | Annexon | HematologyNeurology+2 Rare | NDA Submitted | 6 |
| APGE | Apogee Therapeutics | DermatologyGI/Hepatology+1 Rare | Phase 2 | 9 |
| APVO | Aptevo Therapeutics | Oncology | Phase 1 | 8 |
| RCUS | Arcus Biosciences | DermatologyImmunology+1 | Phase 3 | 6 |
| ARDX | Ardelyx | Renal | Approved | 4 |
| ARTV | Artiva Biotherapeutics | DermatologyImmunology+2 Rare | Phase 2 | 16 |
| ARVN | Arvinas | NeurologyOncology Rare | Approved | 15 |
| ATAI | Atai Beckley | Neurology | Phase 3 | 5 |
| AUTL | Autolus Therapeutics | HematologyImmunology+3 Rare | Approved | 12 |
| BEAM | Beam Therapeutics | HematologyMetabolic+1 Rare | Phase 1 | 7 |
| BCAX | Bicara Therapeutics | Oncology | Phase 3 | 4 |
| BIOA | BioAge Labs | CardiovascularOphthalmology | Phase 1 | 2 |
| BMEA | Biomea Fusion | Metabolic | Phase 2 | 5 |
| BCTX | BriaCell Therapeutics | Oncology | Phase 3 | 8 |
| BBOT | BridgeBio Oncology Therapeutics | Oncology | Phase 1 | 8 |
| CCCC | C4 Therapeutics | Oncology | Phase 2 | 2 |
| CABA | Cabaletta Bio | DermatologyImmunology+2 Rare | Phase 1 | 8 |
| CAPR | Capricor Therapeutics | Neurology Rare | NDA Submitted | 1 |
| CRDL | Cardiol Therapeutics | Cardiovascular Rare | Phase 3 | 4 |
| CRBU | Caribou Biosciences | Oncology | Phase 3 | 4 |
| RNAC | Cartesian Therapeutics | ImmunologyNeurology+1 Rare | Phase 3 | 4 |
| CLDX | Celldex Therapeutics | DermatologyImmunology+1 | Phase 3 | 7 |
| CLRB | Cellectar Biosciences | Oncology | NDA Submitted | 11 |
| IPSC | Century Therapeutics | ImmunologyMetabolic+1 Rare | Phase 1 | 11 |
| CRVO | CervoMed | Neurology Rare | Phase 3 | 5 |
| CGON | CG Oncology | Oncology | NDA Submitted | 1 |
| CING | Cingulate | Neurology | NDA Submitted | 1 |
| CLNN | Clene | Neurology Rare | NDA Submitted | 5 |
| CLYM | Climb Bio | HematologyImmunology+1 Rare | Phase 2 | 7 |
| COGT | Cogent Biosciences | HematologyOncology Rare | NDA Submitted | 6 |
| CGTX | Cognition Therapeutics | Neurology | Phase 2 | 2 |
| CHRS | Coherus Oncology | Oncology | Approved | 4 |
| CMPS | COMPASS Pathways | Neurology | NDA Submitted | 3 |
| CGEN | Compugen | Oncology | Phase 3 | 7 |
| CNTB | Connect Biopharma | Respiratory | Phase 2 | 4 |
| CRVS | Corvus Pharmaceuticals | DermatologyOncology | Phase 3 | 4 |
| CBIO | Crescent Biopharma | Oncology | Phase 1 | 10 |
| CRNX | Crinetics Pharmaceuticals | MetabolicOncology Rare | Approved | 6 |
| CUE | Cue Biopharma | Oncology | Phase 1 | 4 |
| CGEM | Cullinan Therapeutics | HematologyImmunology+2 Rare | NDA Submitted | 10 |
| HELP | Cybin | Neurology | Phase 3 | 3 |
| CYDY | CytoDyn | NeurologyOncology | Phase 2 | 3 |
| CTMX | CytomX Therapeutics | Oncology | Phase 1 | 3 |
| DBVT | DBV Technologies | GI/HepatologyImmunology Rare | NDA Submitted | 3 |
| DFTX | Definium Therapeutics | Neurology | Phase 3 | 4 |
| DYN | Dyne Therapeutics | MetabolicNeurology Rare | NDA Submitted | 10 |
| ELTX | Elicio Therapeutics | Oncology | Phase 2 | 6 |
| ELOX | Eloxx Pharmaceuticals | Renal Rare | Phase 2 | 4 |
| ENTA | Enanta Pharmaceuticals | DermatologyImmunology+1 | Phase 3 | 6 |
| ERAS | Erasca | Oncology | Phase 1 | 4 |
| ETON | Eton Pharmaceuticals | GI/HepatologyMetabolic+1 Rare | Approved | 14 |
| EVMN | Evommune | DermatologyImmunology+1 | Phase 2 | 6 |
| EXEL | Exelixis | CardiovascularOncology | Approved | 21 |
| EYPT | EyePoint | Ophthalmology | Phase 3 | 3 |
| FHTX | Foghorn Therapeutics | Oncology | Phase 1 | 1 |
| FBRX | Forte Biosciences | DermatologyGI/Hepatology | Phase 2 | 3 |
| FBIO | Fortress Biotech | DermatologyHematology+1 Rare | Approved | 12 |
| GUTS | Fractyl Health | Metabolic | Phase 3 | 3 |
| GANX | Gain Therapeutics | MetabolicNeurology Rare | Phase 2 | 5 |
| GHRS | GH Research | NeurologyWomen's Health | Phase 2 | 4 |
| GOSS | Gossamer Bio | Cardiovascular Rare | Phase 3 | 4 |
| GRCE | Grace Therapeutics | Neurology Rare | NDA Submitted | 3 |
| GLSI | Greenwich LifeSciences | Oncology | Phase 3 | 1 |
| IMTX | Immatics | Oncology | Phase 2 | 8 |
| IMMX | Immix Biopharma | Hematology Rare | Phase 2 | 1 |
| IMRX | Immuneering | Oncology | Phase 3 | 5 |
| IMUX | Immunic | GI/HepatologyNeurology | Phase 3 | 4 |
| IBRX | ImmunityBio | Infectious DiseaseOncology | NDA Submitted | 16 |
| IMNM | Immunome | Oncology | NDA Submitted | 9 |
| IMVT | Immunovant | ImmunologyNeurology Rare | Phase 2 | 6 |
| INAB | IN8bio | ImmunologyOncology | Phase 2 | 6 |
| IXHL | Incannex Healthcare | ImmunologyNeurology+1 | Phase 2 | 3 |
| NTLA | Intellia Therapeutics | CardiovascularImmunology Rare | NDA Submitted | 5 |
| JBIO | Jade Biosciences | ImmunologyRenal Rare | Phase 2 | 6 |
| JANX | Janux Therapeutics | Oncology | Phase 1 | 2 |
| KPRX | Kiora Pharmaceuticals | Ophthalmology Rare | Phase 2 | 5 |
| KOD | Kodiak Sciences | Ophthalmology | Phase 3 | 7 |
| KURA | Kura Oncology | MetabolicOncology | Approved | 9 |
| KYMR | Kymera Therapeutics | DermatologyRespiratory Rare | Phase 2 | 4 |
| KYTX | Kyverna Therapeutics | ImmunologyNeurology+1 Rare | NDA Submitted | 7 |
| LRMR | Larimar Therapeutics | Neurology Rare | NDA Submitted | 1 |
| LXEO | Lexeo Therapeutics | CardiovascularNeurology Rare | Phase 1 | 8 |
| LGVN | Longeveron | CardiovascularMetabolic+1 Rare | Phase 2 | 4 |
| MAIA | MAIA Biotechnology | Oncology | Phase 3 | 7 |
| MRKR | Marker Therapeutics | Oncology | Phase 1 | 4 |
| MDNAF | Medicenna Therapeutics | Oncology | Phase 3 | 9 |
| MIST | Milestone Pharmaceuticals | Cardiovascular | Phase 3 | 3 |
| INKT | MiNK Therapeutics | ImmunologyOncology+1 Rare | Phase 2 | 7 |
| GLUE | Monte Rosa Therapeutics | CardiovascularDermatology+2 Rare | Phase 1 | 8 |
| NKTR | Nektar Therapeutics | DermatologyImmunology+2 | Phase 2 | 11 |
| NGEN | NervGen Pharma | Neurology | Phase 1 | 4 |
| NGNE | Neurogene | Neurology Rare | Phase 3 | 1 |
| NKTX | Nkarta | ImmunologyNeurology+1 Rare | Phase 1 | 7 |
| NBP | NovaBridge Biosciences | OncologyOphthalmology | Phase 2 | 6 |
| NRXP | NRX Pharmaceuticals | Neurology | NDA Submitted | 5 |
| NRIX | Nurix Therapeutics | ImmunologyNeurology+1 | Phase 2 | 15 |
| NVCT | Nuvectis Pharma | Oncology | Phase 1 | 3 |
| OCGN | Ocugen | Infectious DiseaseOphthalmology Rare | Phase 3 | 13 |
| OCS | Oculis Holding | NeurologyOphthalmology | Phase 3 | 5 |
| OMER | Omeros | HematologyNeurology+2 Rare | NDA Submitted | 7 |
| IRD | Opus Genetics | Ophthalmology Rare | Approved | 12 |
| ORKA | Oruka Therapeutics | DermatologyImmunology Rare | Phase 2 | 6 |
| OTLK | Outlook Therapeutics | Ophthalmology | NDA Submitted | 3 |
| OVID | Ovid Therapeutics | Neurology Rare | Phase 1 | 6 |
| KTTA | Pasithea Therapeutics | NeurologyOncology Rare | Phase 1 | 4 |
| PEPG | PepGen | Neurology Rare | Phase 2 | 1 |
| CATX | Perspective Therapeutics | Oncology | Phase 1 | 4 |
| PHIO | Phio Pharmaceuticals | Oncology | Phase 1 | 4 |
| PMVP | PMV Pharmaceuticals | Oncology | Phase 2 | 7 |
| PCSA | Processa Pharmaceuticals | GI/HepatologyOncology+1 Rare | Phase 2 | 7 |
| PMN | ProMIS Neurosciences | Neurology Rare | Phase 1 | 6 |
| TARA | Protara Therapeutics | DermatologyMetabolic+1 Rare | Phase 3 | 3 |
| QNRX | Quoin Pharmaceuticals | DermatologyImmunology Rare | Phase 2 | 8 |
| RLMD | Relmada Therapeutics | MetabolicOncology Rare | Phase 2 | 4 |
| REPL | Replimune Group | Oncology | NDA Submitted | 5 |
| RVPH | Reviva Pharmaceuticals | CardiovascularDermatology+2 Rare | Phase 3 | 10 |
| RYTM | Rhythm Pharmaceuticals | Metabolic Rare | Approved | 13 |
| RCKT | Rocket Pharmaceuticals | CardiovascularImmunology Rare | Approved | 4 |
| SGMT | Sagimet Biosciences | DermatologyMetabolic | Phase 3 | 5 |
| SANA | Sana Biotechnology | MetabolicOncology | Phase 1 | 5 |
| SRPT | Sarepta Therapeutics | Neurology Rare | Approved | 10 |
| SCYX | Scynexis | Infectious Disease | Approved | 4 |
| SLS | SELLAS Life Sciences Group | Oncology | Phase 3 | 8 |
| SLDB | Solid Biosciences | CardiovascularNeurology Rare | Phase 3 | 6 |
| SPRB | Spruce Biosciences | Metabolic Rare | Preclinical | 2 |
| SYRE | Spyre Therapeutics | Immunology | Phase 2 | 12 |
| GPCR | Structure Therapeutics | MetabolicRespiratory Rare | Phase 2 | 5 |
| SMMT | Summit Therapeutics | Oncology | Phase 3 | 3 |
| STRO | Sutro Biopharma | Oncology | Phase 1 | 4 |
| TNGX | Tango Therapeutics | Oncology | Phase 1 | 6 |
| TSHA | Taysha Gene Therapies | Neurology Rare | Phase 3 | 4 |
| TECX | Tectonic Therapeutic | Cardiovascular Rare | Phase 2 | 3 |
| TENX | Tenax Therapeutics | Cardiovascular Rare | Phase 3 | 2 |
| TGTX | Tg Therapeutics | Neurology Rare | Approved | 4 |
| TVTX | Travere Therapeutics | MetabolicRenal Rare | Approved | 7 |
| TTRX | Turn Therapeutics | DermatologyInfectious Disease | Phase 3 | 4 |
| TYRA | Tyra Biosciences | MetabolicOncology Rare | Phase 2 | 5 |
| RARE | Ultragenyx Pharmaceutical | CardiovascularGI/Hepatology+2 Rare | Approved | 12 |
| UNCY | Unicycive Therapeutics | Renal | NDA Submitted | 2 |
| QURE | uniQure | HematologyMetabolic+1 Rare | Approved | 6 |
| VNDA | Vanda Pharmaceuticals | CardiovascularDermatology+6 Rare | Approved | 26 |
| VERA | Vera Therapeutics | Infectious DiseaseRenal Rare | Approved | 8 |
| VKTX | Viking Therapeutics | GI/HepatologyMetabolic+1 Rare | Phase 3 | 9 |
| VIR | Vir Biotechnology | Infectious DiseaseOncology Rare | Phase 3 | 10 |
| VRDN | Viridian Therapeutics | Ophthalmology | Approved | 6 |
| VOR | Vor Biopharma | ImmunologyNeurology Rare | Phase 3 | 4 |
| VYGR | Voyager Therapeutics | MetabolicNeurology Rare | Phase 1 | 7 |
| VTVT | vTv Therapeutics | MetabolicRespiratory Rare | Phase 3 | 8 |
| WVE | Wave Life Sciences | MetabolicNeurology+1 Rare | Phase 2 | 5 |
| XNCR | Xencor | HematologyImmunology+4 Rare | Approved | 30 |
| XENE | Xenon Pharmaceuticals | Neurology | Phase 3 | 6 |
| ZBIO | Zenas BioPharma | DermatologyImmunology+1 Rare | NDA Submitted | 11 |
| ZURA | Zura Bio | DermatologyImmunology Rare | Phase 2 | 4 |
| ZYME | Zymeworks | OncologyRespiratory | Approved | 11 |
No companies match those filters.