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Preclinical (110 companies)

Companies with at least one active program at Preclinical.

Ticker Company Therapeutic areas Preclinical programs Lead stage Programs
FDMT 4D Molecular Therapeutics OphthalmologyRespiratory Rare 2 Phase 3 5
ABSI Absci DermatologyGI/Hepatology+1 3 Phase 1 6
ACRS Aclaris Therapeutics DermatologyGI/Hepatology+1 Rare 1 Phase 2 8
ACRV Acrivon Therapeutics Oncology 1 Phase 2 6
ACTU Actuate Therapeutics Oncology 1 Phase 2 4
ABOS Acumen Pharmaceuticals Neurology 2 Phase 2 4
ADAG Adagene Oncology 3 Phase 2 10
ADCT ADC Therapeutics Oncology 1 Approved 5
ACET Adicet Bio ImmunologyNeurology+2 Rare 1 Phase 1 8
ADMA Adma Biologics ImmunologyInfectious Disease Rare 1 Approved 4
AGMB Agomab Therapeutics ImmunologyRespiratory Rare 2 Phase 2 4
AKBA Akebia Therapeutics HematologyOphthalmology+2 Rare 5 Approved 10
ALDX Aldeyra Therapeutics DermatologyOncology+1 Rare 2 NDA Submitted 7
ATHE Alterity Therapeutics Neurology Rare 1 Phase 2 2
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 5
ANIX Anixa Biosciences Oncology 1 Phase 1 3
APGE Apogee Therapeutics DermatologyGI/Hepatology+1 Rare 2 Phase 2 9
APVO Aptevo Therapeutics Oncology 6 Phase 1 8
RCUS Arcus Biosciences DermatologyImmunology+1 2 Phase 3 6
ARDX Ardelyx GI/HepatologyRenal 1 Approved 4
ARVN Arvinas NeurologyOncology Rare 2 Approved 12
ATAI Atai Beckley Neurology 2 Phase 2 5
BLTE Belite Bio MetabolicOphthalmology Rare 4 NDA Submitted 6
BMEA Biomea Fusion MetabolicOncology 1 Phase 2 4
BCTX BriaCell Therapeutics Oncology 5 Phase 3 7
CRDL Cardiol Therapeutics Cardiovascular Rare 1 Phase 3 4
CLRB Cellectar Biosciences Oncology 1 Phase 2 6
IPSC Century Therapeutics ImmunologyMetabolic+1 Rare 5 Phase 1 9
COGT Cogent Biosciences HematologyOncology Rare 1 NDA Submitted 7
CBIO Crescent Biopharma Oncology 1 Phase 2 10
CUE Cue Biopharma ImmunologyOncology 3 Phase 2 6
CGEM Cullinan Therapeutics HematologyImmunology+2 Rare 2 NDA Submitted 10
CTMX CytomX Therapeutics Oncology 1 Phase 1 6
DYN Dyne Therapeutics MetabolicNeurology Rare 8 NDA Submitted 10
EIKN Eikon Therapeutics Oncology 1 Phase 2 13
ELTX Elicio Therapeutics Oncology 3 Phase 2 6
ELOX Eloxx Pharmaceuticals DermatologyRenal Rare 1 Phase 2 4
ENTA Enanta Pharmaceuticals DermatologyImmunology+1 1 Phase 2 6
ENTX Entera Bio GI/HepatologyMetabolic Rare 2 Phase 2 4
ERAS Erasca Oncology 1 Phase 1 3
ETON Eton Pharmaceuticals GI/HepatologyInfectious Disease+2 Rare 1 Approved 14
EXEL Exelixis CardiovascularOncology 1 Approved 22
EYPT EyePoint Ophthalmology 1 Phase 3 3
FHTX Foghorn Therapeutics Oncology 3 Phase 1 5
FBIO Fortress Biotech DermatologyHematology+2 Rare 1 Approved 12
GUTS Fractyl Health Metabolic 2 Phase 3 3
GANX Gain Therapeutics MetabolicNeurology Rare 4 Phase 1 5
IMUX Immunic GI/HepatologyNeurology 1 Phase 3 4
IMNM Immunome Oncology Rare 2 NDA Submitted 9
INAB IN8bio ImmunologyOncology 3 Phase 2 6
INSM Insmed CardiovascularDermatology+2 Rare 1 Approved 9
JBIO Jade Biosciences ImmunologyRenal Rare 2 Phase 2 4
KAPA Kairos Pharma Oncology 7 Phase 2 9
KOD Kodiak Sciences Ophthalmology 2 Phase 3 8
KURA Kura Oncology MetabolicOncology 3 Approved 12
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 1 NDA Submitted 7
LXEO Lexeo Therapeutics CardiovascularNeurology Rare 4 Phase 1 8
LCTX Lineage Cell Therapeutics NeurologyOphthalmology Rare 3 Phase 2 5
LGVN Longeveron CardiovascularMetabolic+1 Rare 1 Phase 2 4
MAIA MAIA Biotechnology Oncology 6 Phase 3 7
MPLT MapLight Therapeutics Neurology 3 Phase 2 6
MRKR Marker Therapeutics Oncology 1 Phase 1 4
MDNAF Medicenna Therapeutics Oncology 6 Phase 2 9
INKT MiNK Therapeutics ImmunologyOncology+1 Rare 3 Phase 2 7
GLUE Monte Rosa Therapeutics CardiovascularDermatology+2 Rare 1 Phase 2 6
NKTR Nektar Therapeutics DermatologyImmunology+2 4 Phase 3 11
NGEN NervGen Pharma Neurology 2 Phase 1 3
NRSN NeuroSense Therapeutics Neurology Rare 1 Phase 2 3
NRXP NRX Pharmaceuticals Neurology 2 NDA Submitted 5
NRIX Nurix Therapeutics ImmunologyNeurology+1 1 Phase 3 16
OCGN Ocugen Infectious DiseaseOphthalmology Rare 3 Phase 3 12
OCS Oculis Holding NeurologyOphthalmology Rare 1 Phase 3 4
OMER Omeros HematologyNeurology+2 Rare 2 Approved 6
IRD Opus Genetics Ophthalmology Rare 5 Approved 14
ORKA Oruka Therapeutics DermatologyImmunology Rare 1 Phase 2 7
OVID Ovid Therapeutics Neurology Rare 2 Phase 2 4
PALI Palisade Bio Immunology 1 Phase 1 3
KTTA Pasithea Therapeutics NeurologyOncology Rare 2 Phase 1 4
PHIO Phio Pharmaceuticals Oncology 1 Phase 1 4
PYPD PolyPid Infectious DiseaseOncology 1 NDA Submitted 2
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare 1 Phase 1 5
PCSA Processa Pharmaceuticals GI/HepatologyImmunology+2 Rare 3 Phase 2 7
PMN ProMIS Neurosciences Neurology Rare 5 Phase 1 6
QNRX Quoin Pharmaceuticals DermatologyImmunology Rare 2 Phase 2 4
RLMD Relmada Therapeutics MetabolicNeurology+1 Rare 1 Phase 2 4
RVPH Reviva Pharmaceuticals CardiovascularDermatology+2 Rare 4 Phase 3 10
SANA Sana Biotechnology MetabolicOncology 3 Phase 1 4
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 1 Approved 10
SCYX Scynexis Infectious DiseaseRenal Rare 1 Approved 5
SLS SELLAS Life Sciences Group Oncology 3 Phase 3 9
SLDB Solid Biosciences CardiovascularNeurology Rare 3 Phase 3 6
SPRB Spruce Biosciences Metabolic Rare 1 Preclinical 2
SYRE Spyre Therapeutics DermatologyImmunology Rare 1 Phase 2 13
GPCR Structure Therapeutics MetabolicRespiratory Rare 1 Phase 3 5
STRO Sutro Biopharma Oncology 3 Phase 1 4
TSHA Taysha Gene Therapies Neurology Rare 2 Phase 3 4
TVTX Travere Therapeutics MetabolicRenal Rare 2 Approved 7
TTRX Turn Therapeutics DermatologyInfectious Disease Rare 2 Phase 2 4
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 1 Approved 12
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 1 Approved 29
PCVX Vaxcyte Infectious Disease 2 Phase 3 6
VERA Vera Therapeutics Infectious DiseaseRenal Rare 1 Approved 6
VIR Vir Biotechnology Infectious DiseaseOncology Rare 1 Phase 3 10
VRDN Viridian Therapeutics ImmunologyOphthalmology 1 Approved 5
VYGR Voyager Therapeutics MetabolicNeurology Rare 8 Phase 1 9
VTVT vTv Therapeutics MetabolicRespiratory Rare 1 Phase 3 8
WVE Wave Life Sciences MetabolicNeurology+1 Rare 1 Phase 2 5
XENE Xenon Pharmaceuticals Neurology Rare 1 Phase 3 8
ZBIO Zenas BioPharma DermatologyImmunology+2 Rare 2 NDA Submitted 11
ZYME Zymeworks OncologyRespiratory 4 Approved 11