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Phase 1 (85 companies)

Companies with at least one active program at Phase 1.

Ticker Company Therapeutic areas Phase 1 programs Lead stage Programs
ABSI Absci Corporation DermatologyGI/HepatologyWomen's Health 3 Phase 1 7
ACRS Aclaris Therapeutics DermatologyRespiratory 2 Phase 2 7
ACRV Acrivon Therapeutics Oncology 2 Phase 2 5
ACTU Actuate Therapeutics Oncology 6 Phase 2 7
ABOS Acumen Pharmaceuticals Neurology 1 Phase 2 2
ADAG Adagene Inc. Oncology 3 Phase 2 9
AKBA Akebia Therapeutics, Inc. HematologyOphthalmologyRenalRespiratory Rare 1 Approved 14
AKTS Aktis Oncology, Inc. Oncology 8 Phase 1 9
ALDX Aldeyra Therapeutics, Inc. DermatologyOncologyOphthalmology Rare 1 NDA Submitted 8
ALLO Allogene Therapeutics, Inc. ImmunologyOncology Rare 4 Phase 2 12
DRTS Alpha Tau Medical Ltd. Oncology 1 Phase 2 5
AMLX Amylyx Pharmaceuticals, Inc. MetabolicNeurology Rare 1 Phase 3 5
ANAB ANAPTYSBIO, INC DermatologyGI/HepatologyImmunologyOncology Rare 3 Approved 6
ANNX Annexon, Inc. HematologyNeurologyOphthalmologyRenal Rare 1 NDA Submitted 6
APGE Apogee Therapeutics, Inc. DermatologyRespiratory 5 Phase 2 8
RCUS Arcus Biosciences, Inc. DermatologyImmunologyOncology 3 Phase 3 7
ARTV Artiva Biotherapeutics, Inc. DermatologyImmunologyOncologyRenal Rare 5 Phase 2 16
ARVN ARVINAS, INC. NeurologyOncology Rare 9 Approved 15
BEAM Beam Therapeutics Inc. HematologyMetabolicRespiratory Rare 4 Phase 1 8
BIOA BioAge Labs, Inc. CardiovascularMetabolicOphthalmology 2 Phase 1 2
BMEA Biomea Fusion, Inc. Metabolic 2 Phase 2 4
BCTX BriaCell Therapeutics Corp. Oncology 1 Phase 3 8
BBOT BridgeBio Oncology Therapeutics, Inc. Oncology 8 Phase 1 8
CCCC C4 Therapeutics, Inc. Oncology 1 Phase 2 2
CABA Cabaletta Bio, Inc. DermatologyImmunologyNeurologyRenal Rare 8 Phase 1 8
CRBU Caribou Biosciences, Inc. ImmunologyOncology 3 Phase 3 4
CLDX Celldex Therapeutics, Inc. DermatologyGI/HepatologyImmunologyRespiratory 1 Phase 3 7
CLRB Cellectar Biosciences, Inc. Oncology 2 NDA Submitted 11
IPSC Century Therapeutics, Inc. ImmunologyMetabolicRenal Rare 5 Phase 1 11
CLYM Climb Bio, Inc. HematologyImmunologyRenal Rare 4 Phase 2 7
COGT Cogent Biosciences, Inc. HematologyOncology Rare 4 NDA Submitted 7
CBIO CRESCENT BIOPHARMA, INC. Oncology 9 Phase 1 10
CRNX Crinetics Pharmaceuticals, Inc. MetabolicOncology Rare 2 Approved 7
CGEM Cullinan Therapeutics, Inc. ImmunologyOncology 6 NDA Submitted 7
CTMX CytomX Therapeutics, Inc. Oncology 2 Phase 1 3
DYN Dyne Therapeutics, Inc. MetabolicNeurology Rare 1 Phase 3 10
ENTA ENANTA PHARMACEUTICALS INC DermatologyImmunologyInfectious Disease 2 Phase 2 6
ERAS Erasca, Inc. Oncology 3 Phase 1 4
ETON Eton Pharmaceuticals, Inc. GI/HepatologyMetabolicRenal Rare 1 Approved 14
FBRX Forte Biosciences, Inc. DermatologyGI/Hepatology 2 Phase 2 3
GUTS FRACTYL HEALTH, INC. Metabolic 1 Phase 3 3
GANX Gain Therapeutics, Inc. MetabolicNeurology Rare 1 Phase 1 5
GHRS GH Research PLC NeurologyWomen's Health 1 Phase 2 4
GRCE Grace Therapeutics, Inc. Neurology Rare 2 Phase 3 3
IMTX Immatics N.V. Oncology 7 Phase 2 8
IMRX Immuneering Corp Oncology 3 Phase 3 5
IBRX ImmunityBio, Inc. Infectious DiseaseOncology 5 Approved 17
INAB IN8BIO, INC. ImmunologyOncology 2 Phase 2 6
JBIO Jade Biosciences, Inc. ImmunologyRenal Rare 1 Phase 1 5
JANX Janux Therapeutics, Inc. Oncology 3 Phase 1 3
KPRX KIORA PHARMACEUTICALS INC Ophthalmology Rare 1 Phase 2 5
KURA Kura Oncology, Inc. MetabolicOncology 7 Phase 1 9
KYMR Kymera Therapeutics, Inc. DermatologyRespiratory 1 Phase 2 5
KYTX Kyverna Therapeutics, Inc. ImmunologyNeurologyRenal Rare 3 NDA Submitted 7
LXEO Lexeo Therapeutics, Inc. CardiovascularNeurology Rare 3 Phase 1 10
MRKR Marker Therapeutics, Inc. Oncology 4 Phase 1 4
MDNAF Medicenna Therapeutics Corp. Oncology 2 Phase 2 9
GLUE Monte Rosa Therapeutics, Inc. CardiovascularDermatologyMetabolicOncology Rare 6 Phase 1 8
NRIX Nurix Therapeutics, Inc. Oncology 10 Phase 2 13
OCGN Ocugen, Inc. Infectious DiseaseOphthalmology Rare 5 Phase 3 13
OMER OMEROS CORP HematologyNeurologyOncologyRespiratory Rare 3 NDA Submitted 7
ORKA Oruka Therapeutics, Inc. DermatologyImmunology Rare 1 Phase 2 6
OVID Ovid Therapeutics Inc. Neurology Rare 5 Phase 1 6
KTTA Pasithea Therapeutics Corp. NeurologyOncology 1 Phase 1 3
CATX Perspective Therapeutics, Inc. Oncology 3 Phase 1 3
PHIO Phio Pharmaceuticals Corp. Oncology 3 Phase 1 4
RYTM RHYTHM PHARMACEUTICALS, INC. Metabolic Rare 2 Approved 13
RCKT ROCKET PHARMACEUTICALS, INC. CardiovascularHematologyImmunology Rare 2 Approved 4
SGMT Sagimet Biosciences Inc. DermatologyMetabolic 2 Phase 3 5
SANA Sana Biotechnology, Inc. MetabolicOncology 1 Phase 1 5
SRPT Sarepta Therapeutics, Inc. Neurology Rare 3 Approved 10
SLDB Solid Biosciences Inc. CardiovascularNeurology Rare 2 Phase 3 6
GPCR Structure Therapeutics Inc. MetabolicRespiratory Rare 2 Phase 2 5
STRO SUTRO BIOPHARMA, INC. Oncology 1 Phase 1 5
TNGX Tango Therapeutics, Inc. Oncology 5 Phase 1 6
RARE Ultragenyx Pharmaceutical Inc. CardiovascularGI/HepatologyMetabolicNeurology Rare 1 Approved 12
QURE uniQure N.V. HematologyMetabolicNeurology Rare 5 Approved 6
VNDA Vanda Pharmaceuticals Inc. CardiovascularDermatologyGI/HepatologyHematologyImmunologyInfectious DiseaseNeurologyOphthalmology Rare 5 Approved 26
VKTX Viking Therapeutics, Inc. GI/HepatologyMetabolicNeurology Rare 1 Phase 3 9
VIR Vir Biotechnology, Inc. Infectious DiseaseOncology Rare 8 Phase 3 10
VRDN Viridian Therapeutics, Inc.\DE Ophthalmology 3 NDA Submitted 6
VYGR Voyager Therapeutics, Inc. MetabolicNeurology Rare 1 Phase 1 7
VTVT vTv Therapeutics Inc. MetabolicRespiratory Rare 1 Phase 3 8
WVE Wave Life Sciences Ltd. MetabolicNeurologyRespiratory Rare 3 Phase 2 5
XENE Xenon Pharmaceuticals Inc. Neurology 3 Phase 3 9