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Small Molecule (70 companies)

Ticker Company Therapeutic areas Programs Lead stage Programs
ACRS Aclaris Therapeutics DermatologyRespiratory 4 Phase 2 7
ACRV Acrivon Therapeutics Oncology 5 Phase 2 5
ACTU Actuate Therapeutics Oncology 3 Phase 2 7
AKBA Akebia Therapeutics, Inc. HematologyOphthalmologyRenalRespiratory Rare 10 Approved 14
ALDX Aldeyra Therapeutics, Inc. DermatologyOncologyOphthalmology Rare 8 NDA Submitted 8
ATHE ALTERITY THERAPEUTICS LTD Neurology Rare 2 Phase 2 2
AMLX Amylyx Pharmaceuticals, Inc. MetabolicNeurology Rare 1 Phase 3 5
ANNX Annexon, Inc. HematologyNeurologyOphthalmologyRenal Rare 1 NDA Submitted 6
RCUS Arcus Biosciences, Inc. DermatologyImmunologyOncology 2 Phase 3 7
ARVN ARVINAS, INC. NeurologyOncology Rare 15 Approved 15
ATAI AtaiBeckley Inc. Neurology 5 Phase 3 5
BIOA BioAge Labs, Inc. CardiovascularMetabolicOphthalmology 2 Phase 1 2
BMEA Biomea Fusion, Inc. Metabolic 4 Phase 2 4
BBOT BridgeBio Oncology Therapeutics, Inc. Oncology 8 Phase 1 8
CCCC C4 Therapeutics, Inc. Oncology 2 Phase 2 2
CRDL Cardiol Therapeutics Inc. Cardiovascular Rare 4 Phase 3 4
CRVO CervoMed Inc. Neurology Rare 5 Phase 2 5
CLNN Clene Inc. Neurology Rare 5 NDA Submitted 5
CLYM Climb Bio, Inc. HematologyImmunologyRenal Rare 1 Phase 2 7
COGT Cogent Biosciences, Inc. HematologyOncology Rare 7 NDA Submitted 7
CGTX COGNITION THERAPEUTICS INC NeurologyOphthalmology 2 Phase 2 2
CMPS COMPASS Pathways plc Neurology 3 NDA Submitted 3
CRVS Corvus Pharmaceuticals, Inc. DermatologyOncology 3 Phase 3 4
CRNX Crinetics Pharmaceuticals, Inc. MetabolicOncology Rare 7 Approved 7
CGEM Cullinan Therapeutics, Inc. ImmunologyOncology 1 NDA Submitted 7
HELP CYBIN INC. Neurology 4 Phase 2 4
DFTX Definium Therapeutics, Inc. Neurology 4 Phase 3 4
ENTA ENANTA PHARMACEUTICALS INC DermatologyImmunologyInfectious Disease 6 Phase 2 6
ERAS Erasca, Inc. Oncology 3 Phase 1 4
ETON Eton Pharmaceuticals, Inc. GI/HepatologyMetabolicRenal Rare 9 Approved 14
EVMN Evommune, Inc. DermatologyImmunologyNeurology 4 Phase 2 6
EYPT EyePoint, Inc. Ophthalmology 3 Phase 3 3
FBIO Fortress Biotech, Inc. DermatologyHematologyMetabolic Rare 8 Approved 14
GANX Gain Therapeutics, Inc. MetabolicNeurology Rare 4 Phase 1 5
GHRS GH Research PLC NeurologyWomen's Health 4 Phase 2 4
GOSS Gossamer Bio, Inc. Cardiovascular Rare 6 Phase 3 6
GRCE Grace Therapeutics, Inc. Neurology Rare 3 Phase 3 3
IMRX Immuneering Corp Oncology 5 Phase 3 5
IBRX ImmunityBio, Inc. Infectious DiseaseOncology 1 Approved 17
IXHL Incannex Healthcare Inc. ImmunologyNeurologyRespiratory 3 Phase 2 3
KPRX KIORA PHARMACEUTICALS INC Ophthalmology Rare 5 Phase 2 5
KURA Kura Oncology, Inc. MetabolicOncology 9 Phase 1 9
KYMR Kymera Therapeutics, Inc. DermatologyRespiratory 5 Phase 2 5
MAIA MAIA Biotechnology, Inc. Oncology 7 Phase 2 7
MIST Milestone Pharmaceuticals Inc. Cardiovascular 3 Phase 3 3
GLUE Monte Rosa Therapeutics, Inc. CardiovascularDermatologyMetabolicOncology Rare 8 Phase 1 8
NRXP NRX Pharmaceuticals, Inc. Neurology 3 NDA Submitted 5
NRIX Nurix Therapeutics, Inc. Oncology 13 Phase 2 13
OMER OMEROS CORP HematologyNeurologyOncologyRespiratory Rare 2 NDA Submitted 7
OVID Ovid Therapeutics Inc. Neurology Rare 6 Phase 1 6
KTTA Pasithea Therapeutics Corp. NeurologyOncology 3 Phase 1 3
PMVP PMV Pharmaceuticals, Inc. Oncology 7 Phase 2 7
PCSA Processa Pharmaceuticals, Inc. GI/HepatologyOncologyRenal Rare 6 Phase 2 8
TARA Protara Therapeutics, Inc. DermatologyMetabolicOncology Rare 1 Phase 3 3
RVPH REVIVA PHARMACEUTICALS HOLDINGS, INC. CardiovascularDermatologyNeurologyRespiratory Rare 10 Phase 3 10
RYTM RHYTHM PHARMACEUTICALS, INC. Metabolic Rare 1 Approved 13
SGMT Sagimet Biosciences Inc. DermatologyMetabolic 4 Phase 3 5
SLS SELLAS Life Sciences Group, Inc. Oncology 3 Phase 3 8
SPRB SPRUCE BIOSCIENCES, INC. MetabolicNeurology Rare 0 Preclinical 2
GPCR Structure Therapeutics Inc. MetabolicRespiratory Rare 5 Phase 2 5
TNGX Tango Therapeutics, Inc. Oncology 6 Phase 1 6
TVTX Travere Therapeutics, Inc. MetabolicRenal Rare 3 Approved 4
TTRX Turn Therapeutics Inc. DermatologyInfectious Disease 3 Phase 2 4
RARE Ultragenyx Pharmaceutical Inc. CardiovascularGI/HepatologyMetabolicNeurology Rare 1 Approved 12
VNDA Vanda Pharmaceuticals Inc. CardiovascularDermatologyGI/HepatologyHematologyImmunologyInfectious DiseaseNeurologyOphthalmology Rare 23 Approved 26
VERA Vera Therapeutics, Inc. Infectious DiseaseRenal Rare 1 NDA Submitted 8
VKTX Viking Therapeutics, Inc. GI/HepatologyMetabolicNeurology Rare 7 Phase 3 9
VYGR Voyager Therapeutics, Inc. MetabolicNeurology Rare 2 Phase 1 7
VTVT vTv Therapeutics Inc. MetabolicRespiratory Rare 8 Phase 3 8
XENE Xenon Pharmaceuticals Inc. Neurology 9 Phase 3 9