HomePhases › Phase 3

Phase 3 (69 companies)

Companies with at least one active program at Phase 3.

Ticker Company Therapeutic areas Phase 3 programs Lead stage Programs
FDMT 4D Molecular Therapeutics OphthalmologyRespiratory Rare 1 Phase 3 5
ACIU AC Immune Neurology Rare 2 Phase 3 11
ALDX Aldeyra Therapeutics DermatologyOncology+1 Rare 2 NDA Submitted 8
ATHE Alterity Therapeutics Neurology Rare 1 Phase 3 2
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 5
ANAB AnaptysBio DermatologyGI/Hepatology+2 Rare 1 Approved 6
ANNX Annexon HematologyNeurology+2 Rare 1 NDA Submitted 6
RCUS Arcus Biosciences DermatologyImmunology+1 3 Phase 3 6
ARDX Ardelyx Renal 1 Approved 4
ARVN Arvinas NeurologyOncology Rare 1 Approved 15
ATAI Atai Beckley Neurology 1 Phase 3 5
BCAX Bicara Therapeutics Oncology 1 Phase 3 4
BCTX BriaCell Therapeutics Oncology 1 Phase 3 8
CRDL Cardiol Therapeutics Cardiovascular Rare 1 Phase 3 4
CRBU Caribou Biosciences Oncology 1 Phase 3 4
RNAC Cartesian Therapeutics ImmunologyNeurology+1 Rare 1 Phase 3 4
CLDX Celldex Therapeutics DermatologyImmunology+1 3 Phase 3 7
CRVO CervoMed Neurology Rare 1 Phase 3 5
CGEN Compugen Oncology 4 Phase 3 7
CRVS Corvus Pharmaceuticals DermatologyOncology 1 Phase 3 4
CRNX Crinetics Pharmaceuticals MetabolicOncology Rare 1 Approved 6
HELP Cybin Neurology 1 Phase 3 3
DFTX Definium Therapeutics Neurology 3 Phase 3 4
ENTA Enanta Pharmaceuticals DermatologyImmunology+1 1 Phase 3 6
ETON Eton Pharmaceuticals GI/HepatologyMetabolic+1 Rare 1 Approved 14
EXEL Exelixis CardiovascularOncology 3 Approved 21
EYPT EyePoint Ophthalmology 2 Phase 3 3
GUTS Fractyl Health Metabolic 1 Phase 3 3
GERN Geron Oncology 1 Approved 3
GOSS Gossamer Bio Cardiovascular Rare 2 Phase 3 4
GLSI Greenwich LifeSciences Oncology 1 Phase 3 1
IMRX Immuneering Oncology 1 Phase 3 5
IMUX Immunic GI/HepatologyNeurology 1 Phase 3 4
NTLA Intellia Therapeutics CardiovascularImmunology Rare 4 NDA Submitted 5
KOD Kodiak Sciences Ophthalmology 5 Phase 3 7
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 1 NDA Submitted 7
MAIA MAIA Biotechnology Oncology 1 Phase 3 7
MDNAF Medicenna Therapeutics Oncology 1 Phase 3 9
MIST Milestone Pharmaceuticals Cardiovascular 1 Phase 3 3
NGNE Neurogene Neurology Rare 1 Phase 3 1
NRXP NRX Pharmaceuticals Neurology 1 NDA Submitted 5
OCGN Ocugen Infectious DiseaseOphthalmology Rare 4 Phase 3 13
OCS Oculis Holding NeurologyOphthalmology 3 Phase 3 5
IRD Opus Genetics Ophthalmology Rare 1 Approved 12
OTLK Outlook Therapeutics Ophthalmology 2 NDA Submitted 3
TARA Protara Therapeutics DermatologyMetabolic+1 Rare 1 Phase 3 3
RVPH Reviva Pharmaceuticals CardiovascularDermatology+2 Rare 1 Phase 3 10
RYTM Rhythm Pharmaceuticals Metabolic Rare 6 Approved 13
SGMT Sagimet Biosciences DermatologyMetabolic 2 Phase 3 5
SRPT Sarepta Therapeutics Neurology Rare 1 Approved 10
SLS SELLAS Life Sciences Group Oncology 1 Phase 3 8
SLDB Solid Biosciences CardiovascularNeurology Rare 1 Phase 3 6
SMMT Summit Therapeutics Oncology 3 Phase 3 3
TSHA Taysha Gene Therapies Neurology Rare 1 Phase 3 4
TENX Tenax Therapeutics Cardiovascular Rare 1 Phase 3 2
TGTX Tg Therapeutics Neurology Rare 1 Approved 4
TVTX Travere Therapeutics MetabolicRenal Rare 1 Approved 7
TTRX Turn Therapeutics DermatologyInfectious Disease 1 Phase 3 4
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 4 Approved 12
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 8 Approved 26
VKTX Viking Therapeutics GI/HepatologyMetabolic+1 Rare 2 Phase 3 9
VIR Vir Biotechnology Infectious DiseaseOncology Rare 1 Phase 3 10
VRDN Viridian Therapeutics Ophthalmology 1 Approved 6
VOR Vor Biopharma ImmunologyNeurology Rare 2 Phase 3 4
VTVT vTv Therapeutics MetabolicRespiratory Rare 1 Phase 3 8
XNCR Xencor HematologyImmunology+4 Rare 2 Approved 30
XENE Xenon Pharmaceuticals Neurology 3 Phase 3 6
ZBIO Zenas BioPharma DermatologyImmunology+1 Rare 2 NDA Submitted 11
ZYME Zymeworks OncologyRespiratory 1 Approved 11