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Amyotrophic Lateral Sclerosis (8 companies)

Companies with an active program in Amyotrophic Lateral Sclerosis.

Ticker Company Therapeutic areas Programs Lead stage Programs
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 5
ANNX Annexon HematologyNeurology+2 Rare 1 NDA Submitted 6
CRVO CervoMed Neurology Rare 1 Phase 3 5
CLNN Clene Neurology Rare 1 NDA Submitted 5
KTTA Pasithea Therapeutics NeurologyOncology Rare 1 Phase 1 4
PMN ProMIS Neurosciences Neurology Rare 1 Phase 1 6
QURE uniQure HematologyMetabolic+1 Rare 1 Approved 6
VYGR Voyager Therapeutics MetabolicNeurology Rare 1 Phase 1 7