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NDA Submitted (31 companies)

Companies with at least one active program at NDA Submitted.

Ticker Company Therapeutic areas NDA Submitted programs Lead stage Programs
ACHV Achieve Life Sciences 1 NDA Submitted 2
ALDX Aldeyra Therapeutics DermatologyOncology+1 Rare 1 NDA Submitted 7
BLTE Belite Bio MetabolicOphthalmology Rare 1 NDA Submitted 6
CAPR Capricor Therapeutics Infectious DiseaseNeurology Rare 1 NDA Submitted 2
CGON CG Oncology Oncology 1 NDA Submitted 1
CING Cingulate Neurology 1 NDA Submitted 1
COGT Cogent Biosciences HematologyOncology Rare 3 NDA Submitted 7
CMPS COMPASS Pathways Neurology 1 NDA Submitted 3
CGEM Cullinan Therapeutics HematologyImmunology+2 Rare 1 NDA Submitted 10
DBVT DBV Technologies Immunology 1 NDA Submitted 2
DYN Dyne Therapeutics MetabolicNeurology Rare 1 NDA Submitted 10
ETON Eton Pharmaceuticals GI/HepatologyInfectious Disease+2 Rare 1 Approved 14
EXEL Exelixis CardiovascularOncology 1 Approved 22
GRCE Grace Therapeutics Neurology 1 NDA Submitted 1
IMNM Immunome Oncology Rare 1 NDA Submitted 9
NTLA Intellia Therapeutics CardiovascularImmunology Rare 1 NDA Submitted 3
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 1 NDA Submitted 7
LRMR Larimar Therapeutics Neurology Rare 1 NDA Submitted 1
NAMS NewAmsterdam Pharma CardiovascularMetabolic+1 3 NDA Submitted 6
NRXP NRX Pharmaceuticals Neurology 2 NDA Submitted 5
IRD Opus Genetics Ophthalmology Rare 1 Approved 14
PYPD PolyPid Infectious DiseaseOncology 1 NDA Submitted 2
RLAY Relay Therapeutics DermatologyOncology Rare 1 NDA Submitted 4
SGMT Sagimet Biosciences DermatologyMetabolic 1 NDA Submitted 3
SMMT Summit Therapeutics Oncology 1 NDA Submitted 4
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 1 Approved 12
UNCY Unicycive Therapeutics Renal 1 NDA Submitted 2
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 4 Approved 29
XNCR Xencor HematologyImmunology+4 Rare 1 Approved 36
ZBIO Zenas BioPharma DermatologyImmunology+2 Rare 1 NDA Submitted 11
ZYME Zymeworks OncologyRespiratory 1 Approved 11