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NDA Submitted (32 companies)

Companies with at least one active program at NDA Submitted.

Ticker Company Therapeutic areas NDA Submitted programs Lead stage Programs
ALDX Aldeyra Therapeutics DermatologyOncology+1 Rare 1 NDA Submitted 8
ANNX Annexon HematologyNeurology+2 Rare 1 NDA Submitted 6
CAPR Capricor Therapeutics Neurology Rare 1 NDA Submitted 1
CLRB Cellectar Biosciences Oncology 1 Approved 11
CGON CG Oncology Oncology 1 NDA Submitted 1
CING Cingulate Neurology 1 NDA Submitted 1
CLNN Clene Neurology Rare 1 NDA Submitted 5
COGT Cogent Biosciences HematologyOncology Rare 2 NDA Submitted 6
CMPS COMPASS Pathways Neurology 1 NDA Submitted 3
CGEM Cullinan Therapeutics HematologyImmunology+2 Rare 1 NDA Submitted 10
DBVT DBV Technologies GI/HepatologyImmunology Rare 1 NDA Submitted 3
DYN Dyne Therapeutics MetabolicNeurology Rare 1 NDA Submitted 10
ETON Eton Pharmaceuticals GI/HepatologyMetabolic+1 Rare 1 Approved 14
EXEL Exelixis CardiovascularOncology 1 Approved 21
GRCE Grace Therapeutics Neurology Rare 1 NDA Submitted 3
IBRX ImmunityBio Infectious DiseaseOncology 1 NDA Submitted 16
IMNM Immunome Oncology 1 NDA Submitted 9
NTLA Intellia Therapeutics CardiovascularImmunology Rare 1 NDA Submitted 5
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 1 NDA Submitted 7
LRMR Larimar Therapeutics Neurology Rare 1 NDA Submitted 1
NRXP NRX Pharmaceuticals Neurology 2 NDA Submitted 5
OMER Omeros HematologyNeurology+2 Rare 1 NDA Submitted 7
IRD Opus Genetics Ophthalmology Rare 1 Approved 12
OTLK Outlook Therapeutics Ophthalmology 1 NDA Submitted 3
REPL Replimune Group Oncology 1 NDA Submitted 5
RYTM Rhythm Pharmaceuticals Metabolic Rare 1 Approved 13
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 2 Approved 12
UNCY Unicycive Therapeutics Renal 1 NDA Submitted 2
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 4 Approved 26
XNCR Xencor HematologyImmunology+4 Rare 1 Approved 30
ZBIO Zenas BioPharma DermatologyImmunology+1 Rare 1 NDA Submitted 11
ZYME Zymeworks OncologyRespiratory 1 Approved 11