Home › Therapeutic areas › Respiratory › Alpha-1 Antitrypsin Deficiency
Alpha-1 Antitrypsin Deficiency (3 companies)
Companies with an active program in Alpha-1 Antitrypsin Deficiency.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| FDMT | 4D Molecular Therapeutics | OphthalmologyRespiratory Rare | 1 | Phase 3 | 5 |
| BEAM | Beam Therapeutics | HematologyMetabolic+1 Rare | 1 | Phase 1 | 7 |
| WVE | Wave Life Sciences | MetabolicNeurology+1 Rare | 1 | Phase 2 | 5 |
No companies match.