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Huntington's Disease (4 companies)

Companies with an active program in Huntington's Disease.

Ticker Company Therapeutic areas Programs Lead stage Programs
ANNX Annexon HematologyNeurology+2 Rare 1 Phase 3 6
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 1 Approved 10
QURE uniQure HematologyMetabolic+1 Rare 1 Approved 4
WVE Wave Life Sciences MetabolicNeurology+1 Rare 1 Phase 2 5