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Friedreich's Ataxia (4 companies)
Companies with an active program in Friedreich's Ataxia.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| LRMR | Larimar Therapeutics | Neurology Rare | 1 | NDA Submitted | 1 |
| LXEO | Lexeo Therapeutics | CardiovascularNeurology Rare | 1 | Phase 1 | 8 |
| SLDB | Solid Biosciences | CardiovascularNeurology Rare | 1 | Phase 3 | 6 |
| VYGR | Voyager Therapeutics | MetabolicNeurology Rare | 1 | Phase 1 | 7 |
No companies match.