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Duchenne Muscular Dystrophy (7 companies)

Companies with an active program in Duchenne Muscular Dystrophy.

Ticker Company Therapeutic areas Programs Lead stage Programs
CAPR Capricor Therapeutics Infectious DiseaseNeurology Rare 1 NDA Submitted 2
DYN Dyne Therapeutics MetabolicNeurology Rare 5 NDA Submitted 10
INSM Insmed CardiovascularDermatology+2 Rare 1 Approved 9
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare 1 Phase 1 5
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 4 Approved 10
SLDB Solid Biosciences CardiovascularNeurology Rare 1 Phase 3 6
WVE Wave Life Sciences MetabolicNeurology+1 Rare 1 Phase 2 5