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Urea Cycle Disorders (2 companies)

Companies with an active program in Urea Cycle Disorders.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare 1 Phase 1 $296M 5
RARE Ultragenyx Pharmaceutical CardiovascularMetabolic+1 Rare 1 Approved $1.57B 10