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Phenylketonuria (2 companies)

Companies with an active program in Phenylketonuria.

Ticker Company Therapeutic areas Programs Lead stage Programs
BEAM Beam Therapeutics Inc. HematologyMetabolicRespiratory Rare 1 Phase 1 8
ETON Eton Pharmaceuticals, Inc. GI/HepatologyMetabolicRenal Rare 1 Approved 14