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Glycogen Storage Disease Type Ia (2 companies)

Companies with an active program in Glycogen Storage Disease Type Ia.

Ticker Company Therapeutic areas Programs Lead stage Programs
BEAM Beam Therapeutics HematologyMetabolic+1 Rare 1 Phase 1 7
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 1 Approved 12