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Glycogen Storage Disease Type Ia (2 companies)
Companies with an active program in Glycogen Storage Disease Type Ia.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| BEAM | Beam Therapeutics | HematologyMetabolic+1 Rare | 1 | Phase 1 | 7 |
| RARE | Ultragenyx Pharmaceutical | CardiovascularGI/Hepatology+2 Rare | 1 | Approved | 12 |
No companies match.