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Classical Homocystinuria (2 companies)
Companies with an active program in Classical Homocystinuria.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| ETON | Eton Pharmaceuticals | GI/HepatologyMetabolic+1 Rare | 1 | Approved | 14 |
| TVTX | Travere Therapeutics | MetabolicRenal Rare | 1 | Approved | 7 |
No companies match.