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Bardet-Biedl Syndrome (2 companies)

Companies with an active program in Bardet-Biedl Syndrome.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
MGTX MeiraGTx ImmunologyMetabolic+2 Rare 2 Phase 3 $864M 16
RYTM Rhythm Pharmaceuticals Metabolic Rare 1 Approved $7.78B 14