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Home › Therapeutic areas › Hematology

Hematology (11 companies · 9 conditions)

Conditions

AL Amyloidosis 2 Rare Cold Agglutinin Disease 1 Rare Hematopoietic Stem Cell Transplant-Associated Thrombotic Microangiopathy 1 Rare Hemophilia 1 Rare Immune Thrombocytopenia 1 Rare Iron Deficiency Anemia 1 Polycythemia Vera 1 Rare Sickle Cell Disease 1 Rare Systemic Mastocytosis 1 Rare

Companies

Ticker Company Therapeutic areas In Hematology Lead stage Programs
AKBA Akebia Therapeutics, Inc. HematologyOphthalmologyRenalRespiratory Rare 1 Approved 14
ANNX Annexon, Inc. HematologyNeurologyOphthalmologyRenal Rare 1 NDA Submitted 6
BEAM Beam Therapeutics Inc. HematologyMetabolicRespiratory Rare 1 Phase 1 8
CLYM Climb Bio, Inc. HematologyImmunologyRenal Rare 1 Phase 2 7
COGT Cogent Biosciences, Inc. HematologyOncology Rare 1 NDA Submitted 7
FBIO Fortress Biotech, Inc. DermatologyHematologyMetabolic Rare 1 Approved 14
IMMX Immix Biopharma, Inc. Hematology Rare 1 Phase 2 1
OMER OMEROS CORP HematologyNeurologyOncologyRespiratory Rare 1 NDA Submitted 7
RCKT ROCKET PHARMACEUTICALS, INC. CardiovascularHematologyImmunology Rare 0 Approved 4
QURE uniQure N.V. HematologyMetabolicNeurology Rare 1 Approved 6
VNDA Vanda Pharmaceuticals Inc. CardiovascularDermatologyGI/HepatologyHematologyImmunologyInfectious DiseaseNeurologyOphthalmology Rare 1 Approved 26