Biotech Distilled
Substack ↗ Subscribe
Subscribe Substack ↗ About

Home › Therapeutic areas › Hematology

Hematology (14 companies · 11 conditions)

Conditions

AL Amyloidosis 3 Rare Immune Thrombocytopenia 2 Rare Paroxysmal Nocturnal Hemoglobinuria 2 Rare Cold Agglutinin Disease 1 Rare Hematopoietic Stem Cell Transplant-Associated Thrombotic Microangiopathy 1 Rare Hemophilia 1 Rare Iron Deficiency Anemia 1 Polycythemia Vera 1 Rare Sickle Cell Disease 1 Rare Systemic Mastocytosis 1 Rare Warm Autoimmune Hemolytic Anemia 1 Rare

Companies

Ticker Company Therapeutic areas In Hematology Lead stage Programs
AKBA Akebia Therapeutics HematologyOphthalmology+2 Rare 1 Approved 10
ANNX Annexon HematologyNeurology+2 Rare 1 Phase 3 6
AUTL Autolus Therapeutics HematologyImmunology+3 Rare 1 Approved 12
BEAM Beam Therapeutics HematologyMetabolic+1 Rare 1 Phase 2 6
CLYM Climb Bio HematologyImmunology+1 Rare 1 Phase 2 7
COGT Cogent Biosciences HematologyOncology Rare 2 NDA Submitted 7
CGEM Cullinan Therapeutics HematologyImmunology+2 Rare 2 NDA Submitted 10
FBIO Fortress Biotech DermatologyHematology+2 Rare 1 Approved 12
IMMX Immix Biopharma Hematology Rare 1 Phase 1 1
NVCT Nuvectis Pharma HematologyOncology+1 Rare 1 Phase 3 8
OMER Omeros HematologyNeurology+2 Rare 1 Approved 6
QURE uniQure HematologyMetabolic+1 Rare 1 Approved 4
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 1 Approved 29
XNCR Xencor HematologyImmunology+4 Rare 2 Approved 36