Biotech Distilled
Substack ↗
Subscribe
Subscribe
Substack ↗
About
Research
Areas
Modalities
Phases
Targets
Track record
Movers
The Lead Compound
Home
›
Targets
› UBE3A antisense
UBE3A antisense
(1 companies · 1 programs)
Companies with an active program directed at UBE3A antisense.
Ultragenyx Pharmaceutical Inc.
RARE
apazunersen
— Angelman Syndrome
Phase 3