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PKR (1 companies · 4 programs)

Companies with an active program directed at PKR.

AGIOS PHARMACEUTICALS, INC. AGIO

  • PYRUKYND — Pyruvate Kinase Deficiency Approved
  • AQVESME — Alpha-Thalassemia Approved
  • AQVESME — Beta-Thalassemia Approved
  • PYRUKYND — Sickle Cell Disease NDA Submitted