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Targets
› HTT
HTT
(3 companies · 3 programs)
Companies with an active program directed at HTT.
Sarepta Therapeutics, Inc.
SRPT
HTT siRNA
— Huntington's Disease
Preclinical
uniQure N.V.
QURE
AMT-130
— Huntington's Disease
Phase 1
Wave Life Sciences Ltd.
WVE
WVE-003
— Huntington's Disease
Phase 1