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The Lead Compound
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› frataxin
frataxin
(3 companies · 3 programs)
Companies with an active program directed at frataxin.
Larimar Therapeutics, Inc.
LRMR
nomlabofusp
— Friedreich's Ataxia
NDA Submitted
Lexeo Therapeutics, Inc.
LXEO
LX2006
— Friedreich Ataxia Cardiomyopathy
Phase 1
Solid Biosciences Inc.
SLDB
SGT-212
— Friedreich's Ataxia
Phase 1