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Targets
› dystrophin
dystrophin
(3 companies · 3 programs)
Companies with an active program directed at dystrophin.
Dyne Therapeutics, Inc.
DYN
zeleciment rostudirsen
— Duchenne Muscular Dystrophy
NDA Submitted
Sarepta Therapeutics, Inc.
SRPT
ELEVIDYS
— Duchenne Muscular Dystrophy
Approved
Solid Biosciences Inc.
SLDB
SGT-003
— Duchenne Muscular Dystrophy
Phase 3