Dyne Therapeutics, Inc. DYN
- zeleciment rostudirsen — Duchenne Muscular Dystrophy NDA Submitted
dystrophin (5 companies · 5 programs)
Companies with an active program directed at dystrophin.
INSMED Inc INSM
- INS1201 — Duchenne Muscular Dystrophy Phase 1
PRECISION BIOSCIENCES INC DTIL
- PBGENE-DMD — Duchenne Muscular Dystrophy Phase 1
Sarepta Therapeutics, Inc. SRPT
- ELEVIDYS — Duchenne Muscular Dystrophy Approved
Solid Biosciences Inc. SLDB
- SGT-003 — Duchenne Muscular Dystrophy Phase 3