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› dystrophin exon 53
dystrophin exon 53
(2 companies · 2 programs)
Companies with an active program directed at dystrophin exon 53.
Dyne Therapeutics, Inc.
DYN
DYNE-253
— Duchenne Muscular Dystrophy
Preclinical
Sarepta Therapeutics, Inc.
SRPT
golodirsen
— Duchenne Muscular Dystrophy
Approved