Dyne Therapeutics, Inc. DYN
- DYNE-302 — Facioscapulohumeral Dystrophy Preclinical
DUX4 (2 companies · 2 programs)
Companies with an active program directed at DUX4.
Sarepta Therapeutics, Inc. SRPT
- SRP-1001 — Facioscapulohumeral Muscular Dystrophy Phase 1