Biotech Distilled
Substack ↗
Subscribe
Subscribe
Substack ↗
About
Research
Areas
Modalities
Phases
Targets
Track record
Movers
The Lead Compound
Home
›
Targets
› ATP7B
ATP7B
(1 companies · 1 programs)
Companies with an active program directed at ATP7B.
Ultragenyx Pharmaceutical Inc.
RARE
rivunatpagene miziparvovec
— Wilson Disease
Phase 3