HomeModalities › Nucleic Acid

Nucleic Acid (12 companies)

Ticker Company Therapeutic areas Programs Lead stage Programs
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 5
BEAM Beam Therapeutics HematologyMetabolic+1 Rare 3 Phase 1 7
DYN Dyne Therapeutics MetabolicNeurology Rare 9 NDA Submitted 10
ELTX Elicio Therapeutics Oncology 1 Phase 2 6
GERN Geron Oncology 3 Approved 3
PEPG PepGen Neurology Rare 1 Phase 2 1
PHIO Phio Pharmaceuticals Oncology 4 Phase 1 4
SRPT Sarepta Therapeutics Neurology Rare 5 Approved 10
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 1 Approved 12
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 2 Approved 26
VIR Vir Biotechnology Infectious DiseaseOncology Rare 1 Phase 3 10
WVE Wave Life Sciences MetabolicNeurology+1 Rare 5 Phase 2 5