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Wilson's Disease (2 companies)

Companies with an active program in Wilson's Disease.

Ticker Company Therapeutic areas Programs Lead stage Programs
ETON Eton Pharmaceuticals, Inc. GI/HepatologyMetabolicRenal Rare 2 Approved 14
RARE Ultragenyx Pharmaceutical Inc. CardiovascularGI/HepatologyMetabolicNeurology Rare 1 Approved 12